Gene therapy: the hope of cure for nearly 7,000 rare diseases. 30 treatments exist.

Half for rare diseases, the other half to treat certain cancers. But in total, 3,000 drugs from gene therapies are under development. International Rare Disease Day takes place this Thursday, February 29, 2024. The AFM-Téléthon is raising money to fight cancer and rare diseases in France. For more information, go to: http://www.afm-télethon.org/.